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Pluripotent stem-cell-based screening uncovers sildenafil as a mitochondrial disease therapy.
New Publication: Annika Zink et. al., Cell. 2026

Annika Zink, Dao-Fu Dai, Annika Wittich, Marie-Thérèse Henke, Giulia Pedrotti, Sonja Heiduschka, Guillem Santamaria, Tancredi Massimo Pentimalli, Christian Brueser, Sofia Notopoulou, Abdul Rahim Umar, Aleksandra Zhaivoron, Laura Petersilie, Caleb Jerred, Jesper Bergmans, Louis Anton Neu, Fabian Schumacher, Jan Keller-Findeisen, Agnieszka Rybak-Wolf, Daniel Stach, Jeanette Reinshagen, Undine Haferkamp, Kim Krieg, Andrea Zaliani, Liliya Euro, Alessia Di Donfrancesco, Chiara Santanatoglia, Enrica Cappellozza, Marta Suarez Cubero, Mario Pavez-Giani, Oleh Bakumenko, David Meierhofer, Alan Foley, Susanne Morales-Gonzalez, Isabella Tolle, Diran Herebian, Daniele Bonesso, Giulia Cecchetto, Sakurako Nagumo Wong, Monica Moresco, Alessandra Maresca, Ilaria Decimo, Francesco De Sanctis, Annalisa Adamo, Merel J W Adjobo-Hermans, Roberto Duchi, Maria Barandalla, Marco Scaglia, Andrea Perota, Cesare Galli, Burkhard Kleuser, Lukas Cyganek, Chris Mühlhausen, Lars Schlotawa, Valeria Tiranti, Ertan Mayatepek, Ildiko Szabo, Chiara La Morgia, Thomas Klopstock, Valerio Carelli, Felix Distelmaier, Andrea Rossi, Nikolaus Rajewsky, Ghanim Ullah, Stefan Jakobs, Christine R Rose, Spyros Petrakis, Frank Edenhofer, Werner J H Koopman, Pawel Lisowski, Anu Suomalainen, Dario Brunetti, Antonio Del Sol, Emanuela Bottani, Ole Pless, Markus Schuelke, Alessandro Prigione.

Pluripotent stem-cell-based screening uncovers sildenafil as a mitochondrial disease therapy.

Cell. 2026 Mar 19;189(6):1656-1679.e42. doi: 10.1016/j.cell.2026.02.008. Epub 2026 Mar 11. PubMed ID: 41819105

 

Further Information:

PubMed

iBrain Collegiates: Sonja Heiduschka, Caleb Jerred, Louis Anton Neu

Prof. Dr. Christine R. Rose

Prof. Dr. Alessandro Prigione

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